Reverse Rett

NLX-101: Change is Possible

NLX-101 is a new drug being developed to treat breathing abnormalities in people with Rett Syndrome. It's possible that beyond breathing, the drug may also improve other core symptoms such as anxiety and movement disorders.

history Campaign has now closed

It ran from 12:00 PM, 4 December 2015 to 5:00 PM, 14 December 2015

open_in_new http://www.reverserett.org.uk

Registered Charity in England and Wales (1136809)

Check mark Match funded

Campaign target

£70,000

Amount raised

£151,478

Donations

116

    Category

  • Health/WellbeingHealth/Wellbeing

    Helping

Location

Situation

Many people with Rett Syndrome struggle daily with breathing irregularities, anxiety and movement disorders. There is currently no established effective treatment for any of these problems.

Solution

NLX-101 is a new drug under development by the pharmaceutical company, Neurolixis. NLX-101 has already been shown to normalise the irregular breathing patterns in Rett mice and has been given Orphan Drug status both in Europe and the US. Through this project, Reverse Rett will help Neurolixis, bring the new drug to the market, by funding the manufacturing and characterisation of clinical supplies of NLX-101 and supporting preparation for submission to the regulatory authorities.